Prime Medicine Clears PM647 IND

Company Prime Medicine Event Type FDA IND Clearance Modality In Vivo Prime Editing (Liver-Directed LNP) Asset PM647 Target SERPINA1 E342K (PiZ Mutation) Disease Area Alpha-1 Antitrypsin Deficiency Summary The FDA cleared Prime Medicine’s IND for PM647, a one-time liver-directed prime editor intended to correct the…

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