FDA Approves Zanvastro for Alexander Disease

Company: Ionis Pharmaceuticals · Drug: Zanvastro (Zilganersen) · Indication: Alexander Disease (Pediatric + Adult) · Regulatory Action: FDA Approval, First-in-Disease · Date: September 3, 2026 Summary FDA approved Ionis’s Zanvastro (zilganersen) for pediatric and adult Alexander disease, creating the first approved therapy for this ultra-rare…